Table 5 Description of the differences between the PedsQLTM3.0DMD self-assessed and proxy-assessed scores, and the reliability indices between the self- and proxy-assessments
Domain | Self-assessment | Proxy-assessment | Mean difference | ICC 2-way mixed effects model | |||
|---|---|---|---|---|---|---|---|
Dimension | N | Mean (SD) | N | Mean (SD) | N | Mean (SD) | [95% CI] |
All ages combined | |||||||
Daily Activities | 81 | 50.4 (26.0) | 81 | 38.1 (24.2) | 81 | -12.3 (14.1) | 0.75 [0.29–0.89] |
Treatment | 81 | 66.8 (19.1) | 81 | 61.1 (23.2) | 81 | -5.7 (22.0) | 0.45 [0.26–0.61] |
Worry | 81 | 81.2 (13.9) | 81 | 56.5 (23.0) | 81 | -24.7 (23.0) | 0.15 [-0.07–0.36] |
Communication | 81 | 56.9 (27.3) | 81 | 46.5 (31.4) | 81 | -10.4 (36.3) | 0.23 [0.02–0.42] |
Group: 8–11 yrs | |||||||
Daily Activities | 49 | 59.5 (24.8) | 49 | 47.4 (24.1) | 49 | -12.0 (13.9) | 0.75 [0.28–0.90] |
Treatment | 49 | 70.0 (18.8) | 49 | 65.5 (18.7) | 49 | -4.5 (18.3) | 0.51 [0.28–0.69] |
Worry | 49 | 82.3 (15.0) | 49 | 57.2 (24.5) | 49 | -25.2 (23.3) | 0.19 [-0.08–0.45] |
Communication | 49 | 52.4 (27.4) | 49 | 44.6 (30.8) | 49 | -7.8 (38.9) | 0.11 [-0.17–0.37] |
Group: 12–18 yrs | |||||||
Daily Activities | 32 | 36.6 (21.6) | 32 | 23.8 (16.3) | 32 | -12.8 (14.5) | 0.59 [0.08–0.82] |
Treatment | 32 | 62.0 (18.9) | 32 | 54.5 (27.8) | 32 | -7.5 (27.0) | 0.34 [0.01–0.61] |
Worry | 32 | 79.6 (12.0) | 32 | 55.4 (20.8) | 32 | -24.1 (22.7) | 0.05 [-0.11–0.27] |
Communication | 32 | 63.8 (26.1) | 32 | 49.3 (32.6) | 32 | -14.5 (32.0) | 0.38 [0.06–0.63] |